Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
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Orphan & Rare Drug Database
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Orphan Drugs Only
idebenone
Orphan
21d
EMA Approved
Imatinib
Orphan
FDA Approved
imatinib mesylate
Orphan
7d
FDA Approved, EMA Approved
imetelstat
Orphan
Cold Chain
FDA Approved (2024)
Imiglucerase
Orphan
Cold Chain
14d
FDA Approved
Interferon gamma-1b
Orphan
Cold Chain
FDA Approved
Interferon-gamma
Orphan
Cold Chain
14d
FDA Approved
Intravenous Immunoglobulin (IVIG)
Orphan
Cold Chain
FDA Approved
Ivosidenib
Orphan
14d
FDA Approved