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OrphanDrug
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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

126 entries
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Orphan Drugs Only
treprostinil
Orphan14dFDA Approved
triheptanoin
Orphan21dFDA Approved, EMA Approved
Vigabatrin
Orphan14dFDA Approved, EMA Approved
Vorasidenib
Orphan14dFDA Approved
vosoritide
Orphan Cold Chain21dFDA Approved
vutrisiran
Orphan Cold Chain18dFDA Approved (2022), EMA Approved (2022)
Page 5 of 5 (126 total)
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