Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
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Orphan Drugs Only
treprostinil
Orphan
14d
FDA Approved
triheptanoin
Orphan
21d
FDA Approved, EMA Approved
Vigabatrin
Orphan
14d
FDA Approved, EMA Approved
Vorasidenib
Orphan
14d
FDA Approved
vosoritide
Orphan
Cold Chain
21d
FDA Approved
vutrisiran
Orphan
Cold Chain
18d
FDA Approved (2022), EMA Approved (2022)
Page 5 of 5 (126 total)
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