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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

284 entries
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Orphan Drugs Only
Ursodeoxycholic acid
3dFDA Approved
Valproic Acid
7dFDA Approved
Vigabatrin
Orphan14dFDA Approved, EMA Approved
Vinblastine
Cold ChainFDA Approved
vitamin A (retinol)
7dFDA Approved
Vitamin B12 (Cobalamin)
vitamin D3
3dFDA Approved
Vitamin K1 (Phytonadione)
3dFDA Approved
Vorasidenib
Orphan14dFDA Approved
vosoritide
Orphan Cold Chain21dFDA Approved
vutrisiran
Orphan Cold Chain18dFDA Approved (2022), EMA Approved (2022)
warfarin
3dFDA Approved
Zidovudine
7dFDA Approved
Zoledronic Acid
Cold Chain10dFDA Approved, EMA Approved
Page 10 of 10 (284 total)
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