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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

284 entries
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Orphan Drugs Only
Somatrogon-ghla
Orphan Cold ChainFDA Approved
Somatropin
Orphan Cold Chain14dFDA Approved
sotalol
3dFDA Approved
Sucralfate
3dFDA Approved, EMA Approved
Sulfadiazine
FDA Approved
Sunitinib
FDA Approved
sunscreen (broad spectrum SPF 50+)
1dFDA Approved
surgical repair
Standard of Care
Tacrolimus
7dFDA Approved
tacrolimus ophthalmic
10dOff-label use
Tafamidis
Orphan10dFDA Approved
Tamoxifen
3dFDA Approved
tamoxifen citrate
5dFDA Approved
Tegaserod
7dFDA Approved
temozolomide
Orphan7dFDA Approved, EMA Approved
Temsirolimus
Orphan Cold ChainFDA Approved
testosterone
5dFDA Approved, EMA Approved
Timolol maleate
5dFDA Approved
tizanidine
5dFDA Approved
tocilizumab
Cold Chain7dFDA Approved, EMA Approved
Tofacitinib
FDA Approved
Tolvaptan
Orphan14dFDA Approved
Topical corticosteroids
2dFDA Approved
Total Parenteral Nutrition
Cold Chain5dFDA Approved
trabectedin
Orphan Cold Chain21dFDA Approved
Trametinib
OrphanFDA Approved
treprostinil
Orphan14dFDA Approved
Tretinoin
FDA Approved
triheptanoin
Orphan21dFDA Approved, EMA Approved
urea
5dFDA Approved
Page 9 of 10 (284 total)
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