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OrphanDrug
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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

13 entries
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Orphan Drugs Only
mannose
Orphan14dInvestigational
mannose-1-phosphate
Orphan Cold Chain30dInvestigational
mavacamten
Orphan14dFDA Approved
mecasermin
Orphan Cold Chain14dFDA Approved, EMA Approved
melatonin
Orphan7dEMA Approved, FDA OTC
Methotrexate
Orphan3dFDA Approved
Metreleptin
Orphan Cold Chain21dFDA Approved
mexiletine
Orphan14dFDA Approved
Midostaurin
Orphan14dFDA Approved
Mifepristone
OrphanFDA Approved
miglustat
Orphan14dFDA Approved, EMA Approved
Mipomersen
Orphan Cold ChainFDA Approved
mitapivat
Orphan10dFDA Approved (2022), EMA Approved (2022)
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