Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
OrphanDrug
Pharma Knowledge Base
Drugs
Diseases
Countries
Pathways
Programs
Suppliers
API Docs
Home
Drugs
Drug Database
13 entries
Filter
Clear
All
A
B
C
D
E
F
G
H
I
J
K
L
M
N
O
P
Q
R
S
T
U
V
W
X
Y
Z
Orphan Drugs Only
mannose
Orphan
14d
Investigational
mannose-1-phosphate
Orphan
Cold Chain
30d
Investigational
mavacamten
Orphan
14d
FDA Approved
mecasermin
Orphan
Cold Chain
14d
FDA Approved, EMA Approved
melatonin
Orphan
7d
EMA Approved, FDA OTC
Methotrexate
Orphan
3d
FDA Approved
Metreleptin
Orphan
Cold Chain
21d
FDA Approved
mexiletine
Orphan
14d
FDA Approved
Midostaurin
Orphan
14d
FDA Approved
Mifepristone
Orphan
FDA Approved
miglustat
Orphan
14d
FDA Approved, EMA Approved
Mipomersen
Orphan
Cold Chain
FDA Approved
mitapivat
Orphan
10d
FDA Approved (2022), EMA Approved (2022)