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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

284 entries
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Orphan Drugs Only
acetaminophen
1dFDA Approved
Acetazolamide
2dFDA Approved
Acitretin
Orphan3dFDA Approved
adalimumab
Cold Chain14dFDA Approved
aflibercept
Cold Chain7dFDA Approved, EMA Approved
Alendronate Sodium
7dFDA Approved, EMA Approved
alglucosidase alfa
Orphan Cold Chain7dFDA Approved, EMA Approved
allopurinol
2dFDA Approved, EMA Approved
alpha-L-iduronidase
Orphan Cold Chain14dFDA Approved, EMA Approved
ambrisentan
Orphan10dFDA Approved
amiodarone
3dFDA Approved
Amnioreduction
OrphanStandard of care
Amphotericin B liposomal
Orphan Cold Chain5dFDA Approved, EMA Approved
Anakinra
Orphan Cold Chain14dFDA Approved
Angiotensin-Converting Enzyme Inhibitors (Enalapril)
2dFDA Approved, EMA Approved
Arsenic trioxide
OrphanFDA Approved
Artificial tears
3dFDA Approved
Artificial tears (Hypromellose)
1dFDA Approved
asciminib
Orphan7dFDA Approved, EMA Approved
ascorbic acid
1dFDA Approved, EMA Approved
aspirin
1dFDA Approved
Ataluren
Orphan21dEMA Approved
atidarsagene autotemcel
Orphan Cold Chain90dEMA Approved
atorvastatin
5dFDA Approved
atropine sulfate
7dFDA Approved
avalglucosidase alfa
Orphan Cold Chain21dFDA Approved (2021), EMA Approved (2021)
Azacitidine
Orphan Cold Chain5dFDA Approved
azathioprine
3dFDA Approved, EMA Approved
Baclofen
7dFDA Approved
baricitinib
Orphan14dFDA Approved, EMA Approved
Page 1 of 10 (284 total)
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