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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

284 entries
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Orphan Drugs Only
cerliponase alfa
Orphan Cold Chain30dFDA Approved, EMA Approved
Cibinqo
7dFDA Approved
Cisplatin
Orphan7dFDA Approved
Clobazam
OrphanFDA Approved
Clomiphene Citrate
FDA Approved
Clonazepam
FDA Approved
cochlear implant
30dFDA Approved, CE Marked
coenzyme Q10
7dDietary Supplement
Colchicine
7dFDA Approved
collagenase clostridium histolyticum
Cold Chain21dFDA Approved
copper histidinate
Orphan Cold Chain14dFDA Approved (Orphan)
cornstarch
3dMedical Food
Corticosteroids
Corticotropin
Orphan Cold ChainFDA Approved
Crizanlizumab
Orphan Cold Chain14dFDA Approved
Crizotinib
Orphan10dFDA Approved
cyanocobalamin
7dFDA Approved
cyclophosphamide
5dFDA Approved
cyclosporine ophthalmic
Orphan5dFDA Approved
Cystagon
OrphanFDA Approved
cysteamine bitartrate
Orphan Cold Chain14dFDA Approved
cytarabine
Cold Chain3dFDA Approved, EMA Approved
Dabrafenib
OrphanFDA Approved
Dapagliflozin
10dFDA Approved
dapsone
7dFDA Approved
deferasirox
Orphan5dFDA Approved, EMA Approved
Deflazacort
Orphan7dFDA Approved
Denosumab
Cold Chain14dFDA Approved
Dexrazoxane
Orphan7dFDA Approved
diacerein
14dEMA Approved
Page 3 of 10 (284 total)
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