Pharma Knowledge Layer · Global Orphan Drug Access Intelligence
OrphanDrug
OrphanDrug
Pharma Knowledge Base
DrugsDiseasesCountriesPathwaysProgramsSuppliersAPI Docs

Navigation

DrugsDiseasesCountriesPathwaysProgramsSuppliersAPI Docs

About

OrphanDrug covers global rare drug access intelligence for 193 countries.

HomeDrugs

Drug Database

284 entries
AllABCDEFGHIJKLMNOPQRSTUVWXYZ
Orphan Drugs Only
Diatrizoate
FDA Approved
Diazepam
FDA Approved
diazoxide
Orphan14dFDA Approved, EMA Approved
diethylcarbamazine
7dFDA Approved (limited availability)
Digoxin
7dFDA Approved
Digoxin Immune Fab
Orphan Cold Chain7dFDA Approved
Diosmin
10dEMA Approved
disopyramide
7dFDA Approved
Dorzolamide
7dFDA Approved
doxorubicin
Cold Chain7dFDA Approved, EMA Approved
Doxycycline
3dFDA Approved
eculizumab
Orphan Cold Chain14dFDA Approved, EMA Approved
Edaravone
Orphan7dFDA Approved
efgartigimod alfa
Orphan Cold Chain14dFDA Approved (2021), EMA Approved (2022), Japan Approved (2022)
eladocagene exuparvovec
Orphan Cold Chain45dEMA Approved (2022)
eliglustat
Orphan10dFDA Approved, EMA Approved
emollients with keratolytics
2dFDA Approved
eplontersen
Orphan Cold Chain21dFDA Approved (2023), EMA Approved (2024)
Epoprostenol
Orphan Cold Chain14dFDA Approved
eptinezumab
Cold Chain30dFDA Approved, Limited Global Availability
eribulin mesylate
Orphan Cold Chain14dFDA Approved
Erythromycin
2dFDA Approved
Erythropoietin
Orphan Cold Chain14dFDA Approved
estradiol
3dFDA Approved, EMA Approved
etanercept
Cold Chain10dFDA Approved
Eteplirsen
Orphan Cold ChainFDA Approved
Everolimus
OrphanFDA Approved
ezetimibe
7dFDA Approved
Fludarabine
Orphan Cold Chain10dFDA Approved
folic acid
2dFDA Approved
Page 4 of 10 (284 total)
← PrevNext →
OrphanDrug — Global Pharma Knowledge Base
DrugsDiseasesCountriesPathwaysProgramsSuppliersAPI Docs|Terms of UsePrivacy Policy