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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

284 entries
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Orphan Drugs Only
Follitropin alfa
Cold ChainFDA Approved
fosdenopterin
Orphan Cold Chain30dFDA Approved (2021), Unregistered in India
furosemide
5dFDA Approved
gabapentin
3dFDA Approved, EMA Approved
galantamine
7dFDA Approved
GM-CSF
Orphan Cold ChainFDA Approved
Gonadotropin
Cold ChainFDA Approved
Growth Hormone
Cold Chain10dFDA Approved
Growth hormone (somatropin)
Orphan Cold Chain14dFDA Approved
Hematopoietic stem cell transplantation
Orphan Cold Chain90dStandard of care
hormone replacement therapy (estrogen/progesterone)
3dFDA Approved
Human Chorionic Gonadotropin (hCG)
Cold ChainFDA Approved
Hydroxychloroquine
7dFDA Approved
hydroxycobalamin
Orphan14dFDA Approved, EMA Approved
Hydroxyurea
FDA Approved
Hypertonic saline
3dFDA Approved
ibuprofen
1dFDA Approved
idebenone
Orphan21dEMA Approved
Imatinib
OrphanFDA Approved
imatinib mesylate
Orphan7dFDA Approved, EMA Approved
Imiglucerase
Orphan Cold Chain14dFDA Approved
Imiquimod
10dFDA Approved
Immunoglobulin
Cold Chain10dFDA Approved
Infliximab
Cold Chain14dFDA Approved
insulin
Cold Chain3dFDA Approved, EMA Approved
Insulin glargine
Cold Chain3dFDA Approved
Interferon gamma-1b
Orphan Cold ChainFDA Approved
Interferon-gamma
Orphan Cold Chain14dFDA Approved
Intravenous Immunoglobulin (IVIG)
Orphan Cold ChainFDA Approved
ivermectin
3dFDA Approved, EMA Approved
Page 5 of 10 (284 total)
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