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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

284 entries
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Orphan Drugs Only
Metronidazole
3dFDA Approved
mexiletine
Orphan14dFDA Approved
Midostaurin
Orphan14dFDA Approved
Mifepristone
OrphanFDA Approved
miglustat
Orphan14dFDA Approved, EMA Approved
minoxidil
5dFDA Approved
Mipomersen
Orphan Cold ChainFDA Approved
mitapivat
Orphan10dFDA Approved (2022), EMA Approved (2022)
Multivitamin with Calcium and Vitamin D
1dOTC - Multiple jurisdictions
mycophenolate mofetil
3dFDA Approved, EMA Approved
N-acetylcysteine
3dFDA Approved
naproxen
1dFDA Approved
nimodipine
5dFDA Approved, EMA Approved
Nitazoxanide
5dFDA Approved
Nitisinone
Orphan21dFDA Approved
nitroglycerin
3dFDA Approved
NovoSeven
Orphan Cold ChainFDA Approved
Nusinersen
Orphan Cold Chain7dUnregistered in India
Occupational and Physical Therapy Support
14dStandard of Care
Octreotide
Orphan Cold Chain10dFDA Approved
Olipudase alfa
Orphan Cold Chain14dFDA Approved
Onasemnogene abeparvovec
Orphan Cold Chain14dNot registered in India
oxybutynin
3dFDA Approved, EMA Approved
Palovarotene
Orphan14dFDA Approved
Pamidronate
7dFDA Approved
Patisiran
Orphan Cold ChainFDA Approved
Pembrolizumab
Cold ChainFDA Approved
phacoemulsification surgery
14dStandard surgical procedure
Phenytoin
5dFDA Approved
physical therapy and orthotic management
Standard of Care
Page 7 of 10 (284 total)
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