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OrphanDrug covers global rare drug access intelligence for 193 countries.

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Drug Database

284 entries
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Orphan Drugs Only
Pravastatin
7dFDA Approved
prednisolone
2dFDA Approved, EMA Approved
prednisone
1dFDA Approved
pregabalin
5dFDA Approved
propranolol
7dFDA Approved
proton pump inhibitors (omeprazole)
3dFDA Approved, EMA Approved
Pyridostigmine
7dFDA Approved
Pyridostigmine Bromide
5dFDA Approved, EMA Approved
Pyridoxine
7dFDA Approved
Pyrimethamine
OrphanFDA Approved
ranibizumab
Cold Chain7dFDA Approved, EMA Approved
Ravulizumab
Orphan Cold ChainFDA Approved
Retinoids (Tretinoin)
3dFDA Approved
Rho(D) immune globulin
Cold Chain7dFDA Approved
Ribavirin
Orphan7dFDA Approved
riboflavin
5dFDA Approved
Risdiplam
Orphan7dUnregistered in India
rituximab
Orphan Cold Chain14dFDA Approved
Romidepsin
Orphan Cold Chain7dFDA Approved
Romiplostim
Orphan Cold Chain7dFDA Approved
ruxolitinib
Orphan7dFDA Approved
Sacrosidase
OrphanFDA Approved
salicylic acid
3dFDA Approved
sclerostin antibody
Cold Chain7dFDA Approved, EMA Approved
selumetinib
Orphan14dFDA Approved, EMA Approved
Sildenafil
7dFDA Approved
sirolimus
Orphan5dFDA Approved, EMA Approved
Sodium Bicarbonate
Sodium Phenylbutyrate
OrphanFDA Approved
Sodium Thiosulfate
Page 8 of 10 (284 total)
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