Pharma Knowledge Layer · Global Orphan Drug Access Intelligence

Pharma Knowledge Base

Drug Database

126 entries

All A B C D E F G H I J K L M N O P Q R S T U V W X Y Z

Orphan Drugs Only

Hematopoietic stem cell transplantation

Orphan Cold Chain90dStandard of care

hydroxycobalamin

Orphan14dFDA Approved, EMA Approved

Orphan21dEMA Approved

OrphanFDA Approved

imatinib mesylate

Orphan7dFDA Approved, EMA Approved

Orphan Cold Chain14dFDA Approved

Interferon gamma-1b

Orphan Cold ChainFDA Approved

Interferon-gamma

Orphan Cold Chain14dFDA Approved

Intravenous Immunoglobulin (IVIG)

Orphan Cold ChainFDA Approved

Orphan14dFDA Approved

Orphan5dFDA Approved, EMA Approved

Orphan Cold Chain14dFDA Approved

Orphan Cold Chain14dFDA Approved, EMA Approved

Laser photocoagulation therapy

OrphanFDA Approved

OrphanFDA Approved

Orphan21dFDA Approved, EMA Approved

loncastuximab tesirine

Orphan Cold Chain14dFDA Approved (2021), EMA Approved (2022)

Orphan Cold ChainFDA Approved, EMA Approved

Orphan Cold Chain10dFDA Approved, EMA Approved

Orphan14dInvestigational

mannose-1-phosphate

Orphan Cold Chain30dInvestigational

Orphan14dFDA Approved

Orphan Cold Chain14dFDA Approved, EMA Approved

Orphan7dEMA Approved, FDA OTC

Orphan3dFDA Approved

Orphan Cold Chain21dFDA Approved

Orphan14dFDA Approved

Orphan14dFDA Approved

OrphanFDA Approved

Orphan14dFDA Approved, EMA Approved

Page 3 of 5 (126 total)

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